About 

In 2019 at age 15 months Michael was diagnosed with an 

ultra-rare condition called SPG50 disease caused by a single gene AP4M1. 

 

Doctors explained that there was no cure, nor any treatment options for this rare neurological degenerative disorder which would slowly take away Michael's cognitive and physical abilities similar to Cerebral Palsy but progressive.

 

His Parents Terry & Georgia are unwilling to accept this prognosis and are working to fund gene therapy to cure or at least stop the progression of this terrible disease not just for Michael but all children affected.

With your support by October 2021 we will be ready to start a clinical trial, but we need your help!

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